Near-complete elimination of mutant mtDNA by iterative or dynamic dose-controlled treatment with mtZFNs

Gammage PA., Gaude E., Van Haute L., Rebelo-Guiomar P., Jackson CB., Rorbach J., Pekalski ML., Robinson AJ., Charpentier M., Concordet J-P., Frezza C., Minczuk M.

DOI

10.1093/nar/gkw676

Type

Journal article

Journal

Nucleic Acids Research

Publisher

Oxford University Press (OUP)

Publication Date

19/09/2016

Volume

44

Pages

7804 - 7816

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